Cystic Fibrosis (Respiratory) – Drugs In Development, 2021

Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Cystic Fibrosis – Drugs In Development, 2021, provides an overview of the Cystic Fibrosis (Respiratory) pipeline landscape.

Cystic fibrosis (CF) is an inherited disease that causes mucus to build up and clog some of the body’s organs, particularly the lungs and pancreas. Cystic fibrosis affects the cells that produce mucus, sweat and digestive juices.  Symptoms include wheezing, breathlessness, repeated lung infections, inflamed nasal passages or a stuffy nose and severe constipation. Risk factors include family history and race (Northern European ancestry). Treatment includes antibiotics, mucus-thinning, bronchodilators and oral pancreatic enzymes.

Report Highlights

Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Cystic Fibrosis – Drugs In Development, 2021, provides comprehensive information on the therapeutics under development for Cystic Fibrosis (Respiratory), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Cystic Fibrosis (Respiratory) pipeline guide also reviews of key players involved in therapeutic development for Cystic Fibrosis and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical, Discovery and Unknown stages are 3, 3, 32, 18, 2, 75, 39 and 2 respectively. Similarly, the Universities portfolio in Phase II, Preclinical, Discovery and Unknown stages comprises 1, 6, 8 and 1 molecules, respectively.

Cystic Fibrosis (Respiratory) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope

– The pipeline guide provides a snapshot of the global therapeutic landscape of Cystic Fibrosis (Respiratory).

– The pipeline guide reviews pipeline therapeutics for Cystic Fibrosis (Respiratory) by companies and universities/research institutes based on information derived from company and industry-specific sources.

– The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.

– The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.

– The pipeline guide reviews key companies involved in Cystic Fibrosis (Respiratory) therapeutics and enlists all their major and minor projects.

– The pipeline guide evaluates Cystic Fibrosis (Respiratory) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.

– The pipeline guide encapsulates all the dormant and discontinued pipeline projects.

– The pipeline guide reviews latest news related to pipeline therapeutics for Cystic Fibrosis (Respiratory)

Reasons to buy

- Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.

- Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.

- Find and recognize significant and varied types of therapeutics under development for Cystic Fibrosis (Respiratory).

- Classify potential new clients or partners in the target demographic.

- Develop tactical initiatives by understanding the focus areas of leading companies.

- Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.

- Formulate corrective measures for pipeline projects by understanding Cystic Fibrosis (Respiratory) pipeline depth and focus of Indication therapeutics.

- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.

- Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.

Companies mentioned

4D Molecular Therapeutics Inc

AbbVie Inc

Abeona Therapeutics Inc

Aceragen Inc

Affinia Therapeutics

Agile Sciences Inc

AiCuris AG

Airbase Breathing Co LLC

Airway Therapeutics LLC

Alaxia SAS

AlgiPharma AS

Antabio SAS

Arch Biopartners Inc

Arcturus Therapeutics Holdings Inc

Armata Pharmaceuticals

Arrevus Inc

Arrowhead Pharmaceuticals Inc

Atlantic Healthcare Plc

Avidin Biotechnology Ltd

BioAegis Therapeutics Inc

Biofilm Pharma

Biolytx Pharmaceuticals Corp

BiomX Inc

Boehringer Ingelheim International GmbH

Boston Pharmaceuticals Inc

Breathe Easy Therapeutics Ltd

BridgeBio Pharma Inc

Calista Therapeutics Inc

Calithera Biosciences Inc

Catabasis Pharmaceuticals Inc

Chiesi Farmaceutici SpA

Cilian AG

Clarametyx Biosciences Inc

ContraFect Corp

Copernicus Therapeutics Inc

CRISPR Therapeutics AG

CrowdOut Therapeutics

CSA Biotechnologies LLC

Cyclacel Pharmaceuticals Inc

Cyclenium Pharma Inc

Daiichi Sankyo Co Ltd

Destiny Pharma Plc

DiscoveryBiomed Inc

Editas Medicine Inc

Eloxx Pharmaceuticals Inc

EmphyCorp Inc

EnBiotix Inc

enGene Inc

Enterprise Therapeutics Ltd

Entrinsic Bioscience Inc

Evaxion Biotech ApS

Evotec SE

Exotect LLC

F. Hoffmann-La Roche Ltd

Feldan Therapeutics Inc

Felix Biotechnology Inc

Galapagos NV

Galenus Therapeutics Inc

Generation Bio Co

Genzyme Corp

Helperby Therapeutics Group Ltd

Horizon Therapeutics Plc

Hunterian Medicine LLC

Icagen Inc

Immun System IMS AB

Insmed Inc

Invion Ltd

Ionis Pharmaceuticals Inc

Kamada Pharmaceuticals

Kither Biotech Srl

Krystal Biotech Inc

Lakewood-Amedex Inc

Lamellar Biomedical Ltd

Laurent Pharmaceuticals Inc

MannKind Corp

Mariposa Health Ltd

Microbion Corp

Mucokinetica Ltd

Nabriva Therapeutics Plc

Nanogenics Ltd

Neupharma Srl

New Amsterdam Sciences Inc

Novabiotics Ltd

Omnispirant Ltd

Orphomed Inc

OrPro Therapeutics Inc

Oryn Therapeutics

Parion Sciences Inc

Pharmaero ApS

PhaseBio Pharmaceuticals Inc

Polyphor Ltd

Progenra Inc

Prolong Pharmaceuticals LLC

Pulmatrix Inc

PureIMS BV

Pylum Biosciences Inc

RAGE Biotech Pty Ltd

Rare Partners Srl

Recode Therapeutics Inc

Renovion Inc

Respirion Pharmaceuticals Pty Ltd

Riptide Bioscience Inc

San Rocco Therapeutics LLC

Santhera Pharmaceuticals Holding AG

Sarcomed AB

SciBac Inc

Sequoia Sciences Inc

Shape Therapeutics Inc

Silurian Pharmaceuticals Inc

SOLA Biosciences LLC

SolAeroMed Inc

Specific Biologics Inc

Spirovant Sciences Inc

SpliSense Ltd

Synedgen Inc

Synovo GmbH

Synspira Therapeutics Inc

Takeda Pharmaceutical Co Ltd

Tavanta Therapeutics Inc

TGV-Inhalonix Inc

Therapeutic Systems Research Laboratories Inc

Translate Bio Inc

Vast Therapeutics Inc

Vectura Group Plc

Vera Therapeutics Inc

Verona Pharma Plc

Vertex Pharmaceuticals Inc

VGSK Technologies Inc

Vironika LLC

Yumanity Therapeutics Inc

Zambon Co SpA

Zata Pharmaceuticals Inc

Table of Contents

Table of Contents

Introduction

Cystic Fibrosis - Overview

Cystic Fibrosis - Therapeutics Development

Cystic Fibrosis - Therapeutics Assessment

Cystic Fibrosis - Companies Involved in Therapeutics Development

Cystic Fibrosis - Drug Profiles

Cystic Fibrosis - Dormant Projects

Cystic Fibrosis - Discontinued Products

Cystic Fibrosis - Product Development Milestones

Appendix

List of Tables

List of Tables

Number of Products under Development for Cystic Fibrosis, 2021

Number of Products under Development by Companies, 2021

Number of Products under Development by Universities/Institutes, 2021

Products under Development by Companies, 2021

Products under Development by Universities/Institutes, 2021

Number of Products by Stage and Target, 2021

Number of Products by Stage and Mechanism of Action, 2021

Number of Products by Stage and Route of Administration, 2021

Number of Products by Stage and Molecule Type, 2021

Cystic Fibrosis – Pipeline by 4D Molecular Therapeutics Inc, 2021

Cystic Fibrosis – Pipeline by AbbVie Inc, 2021

Cystic Fibrosis – Pipeline by Abeona Therapeutics Inc, 2021

Cystic Fibrosis – Pipeline by Aceragen Inc, 2021

Cystic Fibrosis – Pipeline by Affinia Therapeutics, 2021

Cystic Fibrosis – Pipeline by Agile Sciences Inc, 2021

Cystic Fibrosis – Pipeline by AiCuris AG, 2021

Cystic Fibrosis – Pipeline by Airbase Breathing Co LLC, 2021

Cystic Fibrosis – Pipeline by Airway Therapeutics LLC, 2021

Cystic Fibrosis – Pipeline by Alaxia SAS, 2021

Cystic Fibrosis – Pipeline by AlgiPharma AS, 2021

Cystic Fibrosis – Pipeline by Antabio SAS, 2021

Cystic Fibrosis – Pipeline by Arch Biopartners Inc, 2021

Cystic Fibrosis – Pipeline by Arcturus Therapeutics Holdings Inc, 2021

Cystic Fibrosis – Pipeline by Armata Pharmaceuticals, 2021

Cystic Fibrosis – Pipeline by Arrevus Inc, 2021

Cystic Fibrosis – Pipeline by Arrowhead Pharmaceuticals Inc, 2021

Cystic Fibrosis – Pipeline by Atlantic Healthcare Plc, 2021

Cystic Fibrosis – Pipeline by Avidin Biotechnology Ltd, 2021

Cystic Fibrosis – Pipeline by BioAegis Therapeutics Inc, 2021

Cystic Fibrosis – Pipeline by Biofilm Pharma, 2021

Cystic Fibrosis – Pipeline by Biolytx Pharmaceuticals Corp, 2021

Cystic Fibrosis – Pipeline by BiomX Inc, 2021

Cystic Fibrosis – Pipeline by Boehringer Ingelheim International GmbH, 2021

Cystic Fibrosis – Pipeline by Boston Pharmaceuticals Inc, 2021

Cystic Fibrosis – Pipeline by Breathe Easy Therapeutics Ltd, 2021

Cystic Fibrosis – Pipeline by BridgeBio Pharma Inc, 2021

Cystic Fibrosis – Pipeline by Calista Therapeutics Inc, 2021

Cystic Fibrosis – Pipeline by Calithera Biosciences Inc, 2021

Cystic Fibrosis – Pipeline by Catabasis Pharmaceuticals Inc, 2021

Cystic Fibrosis – Pipeline by Chiesi Farmaceutici SpA, 2021

Cystic Fibrosis – Pipeline by Cilian AG, 2021

Cystic Fibrosis – Pipeline by Clarametyx Biosciences Inc, 2021

Cystic Fibrosis – Pipeline by ContraFect Corp, 2021

Cystic Fibrosis – Pipeline by Copernicus Therapeutics Inc, 2021

Cystic Fibrosis – Pipeline by CRISPR Therapeutics AG, 2021

Cystic Fibrosis – Pipeline by CrowdOut Therapeutics, 2021

Cystic Fibrosis – Pipeline by CSA Biotechnologies LLC, 2021

Cystic Fibrosis – Pipeline by Cyclacel Pharmaceuticals Inc, 2021

Cystic Fibrosis – Pipeline by Cyclenium Pharma Inc, 2021

Cystic Fibrosis – Pipeline by Daiichi Sankyo Co Ltd, 2021

Cystic Fibrosis – Pipeline by Silurian Pharmaceuticals Inc, 2021

Cystic Fibrosis – Pipeline by SOLA Biosciences LLC, 2021

Cystic Fibrosis – Pipeline by SolAeroMed Inc, 2021

Cystic Fibrosis – Pipeline by Specific Biologics Inc, 2021

Cystic Fibrosis – Pipeline by Spirovant Sciences Inc, 2021

Cystic Fibrosis – Pipeline by SpliSense Ltd, 2021

Cystic Fibrosis – Pipeline by Synedgen Inc, 2021

Cystic Fibrosis – Pipeline by Synovo GmbH, 2021

Cystic Fibrosis – Pipeline by Synspira Therapeutics Inc, 2021

Cystic Fibrosis – Pipeline by Takeda Pharmaceutical Co Ltd, 2021

Cystic Fibrosis – Pipeline by Tavanta Therapeutics Inc, 2021

Cystic Fibrosis – Pipeline by TGV-Inhalonix Inc, 2021

Cystic Fibrosis – Pipeline by Therapeutic Systems Research Laboratories Inc, 2021

Cystic Fibrosis – Pipeline by Translate Bio Inc, 2021

Cystic Fibrosis – Pipeline by Vast Therapeutics Inc, 2021

Cystic Fibrosis – Pipeline by Vectura Group Plc, 2021

Cystic Fibrosis – Pipeline by Vera Therapeutics Inc, 2021

Cystic Fibrosis – Pipeline by Verona Pharma Plc, 2021

Cystic Fibrosis – Pipeline by Vertex Pharmaceuticals Inc, 2021

Cystic Fibrosis – Pipeline by VGSK Technologies Inc, 2021

Cystic Fibrosis – Dormant Projects, 2021

Cystic Fibrosis – Discontinued Products, 2021

List of Figures

List of Figures

Number of Products under Development for Cystic Fibrosis, 2021

Number of Products under Development by Companies, 2021

Number of Products under Development by Universities/Institutes, 2021

Number of Products by Top 10 Targets, 2021

Number of Products by Stage and Top 10 Targets, 2021

Number of Products by Top 10 Mechanism of Actions, 2021

Number of Products by Stage and Top 10 Mechanism of Actions, 2021

Number of Products by Top 10 Routes of Administration, 2021

Number of Products by Stage and Top 10 Routes of Administration, 2021

Number of Products by Top 10 Molecule Types, 2021

Number of Products by Stage and Top 10 Molecule Types, 2021

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