Spinal Muscular Atrophy (SMA) (Central Nervous System) – Drugs In Development, 2021

Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Spinal Muscular Atrophy – Drugs In Development, 2021, provides an overview of the Spinal Muscular Atrophy (Central Nervous System) pipeline landscape.

Spinal muscular atrophy (SMA) is a genetic disease that attacks nerve cells, called motor neurons, in the spinal cord. These critically important cells are responsible for supplying electrical and chemical messages to muscle cells. Without the proper input from the motor neurons, muscle cells cannot function properly. The muscle cells will, therefore, become much smaller (atrophy) and will produce symptoms of muscle weakness. This can affect walking, crawling, breathing, swallowing, and head and neck control.

Report Highlights

Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Spinal Muscular Atrophy – Drugs In Development, 2021, provides comprehensive information on the therapeutics under development for Spinal Muscular Atrophy (Central Nervous System), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Spinal Muscular Atrophy (Central Nervous System) pipeline guide also reviews of key players involved in therapeutic development for Spinal Muscular Atrophy (SMA) and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical and Discovery stages are 2, 1, 4, 4, 1, 20 and 5 respectively. Similarly, the Universities portfolio in Phase II, Preclinical and Discovery stages comprises 2, 8 and 2 molecules, respectively.

Spinal Muscular Atrophy (Central Nervous System) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope

– The pipeline guide provides a snapshot of the global therapeutic landscape of Spinal Muscular Atrophy (Central Nervous System).

– The pipeline guide reviews pipeline therapeutics for Spinal Muscular Atrophy (Central Nervous System) by companies and universities/research institutes based on information derived from company and industry-specific sources.

– The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.

– The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.

– The pipeline guide reviews key companies involved in Spinal Muscular Atrophy (Central Nervous System) therapeutics and enlists all their major and minor projects.

– The pipeline guide evaluates Spinal Muscular Atrophy (Central Nervous System) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.

– The pipeline guide encapsulates all the dormant and discontinued pipeline projects.

– The pipeline guide reviews latest news related to pipeline therapeutics for Spinal Muscular Atrophy (Central Nervous System)

Reasons to buy

- Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.

- Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.

- Find and recognize significant and varied types of therapeutics under development for Spinal Muscular Atrophy (Central Nervous System).

- Classify potential new clients or partners in the target demographic.

- Develop tactical initiatives by understanding the focus areas of leading companies.

- Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.

- Formulate corrective measures for pipeline projects by understanding Spinal Muscular Atrophy (Central Nervous System) pipeline depth and focus of Indication therapeutics.

- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.

- Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.

Companies mentioned

Alcyone Therapeutics Inc

Allianz Pharmascience Ltd (Inactive)

AlphaCognition Inc

Anima Biotech Inc

Apteeus

Biogen Inc

Bioleaders Corp

BioMarin Pharmaceutical Inc

Biophytis SA

Cell Tech Pharmed Co

Enzerna Biosciences LLC

F. Hoffmann-La Roche Ltd

GNT Pharma Co Ltd

Imago Pharmaceuticals Inc

Kowa Co Ltd

Myocea Inc

Neurotune AG

Table of Contents

Table of Contents

Introduction

Spinal Muscular Atrophy (SMA) - Overview

Spinal Muscular Atrophy (SMA) - Therapeutics Development

Spinal Muscular Atrophy (SMA) - Therapeutics Assessment

Spinal Muscular Atrophy (SMA) - Companies Involved in Therapeutics Development

Spinal Muscular Atrophy (SMA) - Drug Profiles

Spinal Muscular Atrophy (SMA) - Dormant Projects

Spinal Muscular Atrophy (SMA) - Discontinued Products

Spinal Muscular Atrophy (SMA) - Product Development Milestones

Appendix

List of Tables

List of Tables

Number of Products under Development for Spinal Muscular Atrophy (SMA), 2021

Number of Products under Development by Companies, 2021

Number of Products under Development by Universities/Institutes, 2021

Products under Development by Companies, 2021

Products under Development by Universities/Institutes, 2021

Number of Products by Stage and Target, 2021

Number of Products by Stage and Mechanism of Action, 2021

Number of Products by Stage and Route of Administration, 2021

Number of Products by Stage and Molecule Type, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Alcyone Therapeutics Inc, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Allianz Pharmascience Ltd (Inactive), 2021

Spinal Muscular Atrophy (SMA) – Pipeline by AlphaCognition Inc, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Anima Biotech Inc, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Apteeus, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Biogen Inc, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Bioleaders Corp, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by BioMarin Pharmaceutical Inc, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Biophytis SA, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Cell Tech Pharmed Co, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Enzerna Biosciences LLC, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by F. Hoffmann-La Roche Ltd, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by GNT Pharma Co Ltd, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Imago Pharmaceuticals Inc, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Kowa Co Ltd, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Myocea Inc, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Neurotune AG, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by NMD Pharma AS, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Novartis AG, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Novartis Gene Therapies, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by Ono Pharmaceutical Co Ltd, 2021

Spinal Muscular Atrophy (SMA) – Pipeline by PTC Therapeutics Inc, 2021

Spinal Muscular Atrophy (SMA) – Dormant Projects, 2021

Spinal Muscular Atrophy (SMA) – Discontinued Products, 2021

List of Figures

List of Figures

Number of Products under Development for Spinal Muscular Atrophy (SMA), 2021

Number of Products under Development by Companies, 2021

Number of Products under Development by Universities/Institutes, 2021

Number of Products by Top 10 Targets, 2021

Number of Products by Stage and Top 10 Targets, 2021

Number of Products by Top 10 Mechanism of Actions, 2021

Number of Products by Stage and Top 10 Mechanism of Actions, 2021

Number of Products by Routes of Administration, 2021

Number of Products by Stage and Routes of Administration, 2021

Number of Products by Molecule Types, 2021

Number of Products by Stage and Molecule Types, 2021

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