Thalassemia (Hematology) – Drugs In Development, 2021

Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Thalassemia – Drugs In Development, 2021, provides an overview of the Thalassemia (Hematological Disorders) pipeline landscape.

Thalassemia is a group of inherited blood disorders that affect the body's ability to produce hemoglobin and red blood cells. Symptoms include fussiness, paleness, frequent infections, failure to thrive, poor appetite and jaundice. Predisposing factors include family history. Treatment includes blood transfusions and bone marrow transplant.

Report Highlights

Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Thalassemia – Drugs In Development, 2021, provides comprehensive information on the therapeutics under development for Thalassemia (Hematological Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Thalassemia (Hematological Disorders) pipeline guide also reviews of key players involved in therapeutic development for Thalassemia and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Phase III, Phase II, Phase I, Preclinical and Discovery stages are 1, 19, 6, 19 and 6 respectively. Similarly, the Universities portfolio in Phase II, Preclinical and Discovery stages comprises 1, 3 and 1 molecules, respectively.

Thalassemia (Hematological Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope

– The pipeline guide provides a snapshot of the global therapeutic landscape of Thalassemia (Hematological Disorders).

– The pipeline guide reviews pipeline therapeutics for Thalassemia (Hematological Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.

– The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.

– The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.

– The pipeline guide reviews key companies involved in Thalassemia (Hematological Disorders) therapeutics and enlists all their major and minor projects.

– The pipeline guide evaluates Thalassemia (Hematological Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.

– The pipeline guide encapsulates all the dormant and discontinued pipeline projects.

– The pipeline guide reviews latest news related to pipeline therapeutics for Thalassemia (Hematological Disorders)

Reasons to buy

- Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.

- Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.

- Find and recognize significant and varied types of therapeutics under development for Thalassemia (Hematological Disorders).

- Classify potential new clients or partners in the target demographic.

- Develop tactical initiatives by understanding the focus areas of leading companies.

- Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.

- Formulate corrective measures for pipeline projects by understanding Thalassemia (Hematological Disorders) pipeline depth and focus of Indication therapeutics.

- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.

- Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.

Companies mentioned

Abfero Pharmaceuticals Inc

Acceleron Pharma Inc

Agios Pharmaceuticals Inc

Aruvant Sciences Inc

ASC Therapeutics Inc

Beam Therapeutics Inc

Bellicum Pharmaceuticals Inc

BGI Genomics Co Ltd

Biomac Lifesciences Pvt Ltd

bluebird bio Inc

Cell Source Inc

Cetya Therapeutics Inc

CRISPR Therapeutics AG

CSL Ltd

Disc Medicine Inc

DisperSol Technologies LLC

EdiGene Inc

Editas Medicine Inc

EmeraMed Ltd

Forma Therapeutics Inc

Fulcrum Therapeutics Inc

Gamida Cell Ltd

Gilead Sciences Inc

Hangzhou Zede Pharmaceutical Technology Co Ltd

Imago BioSciences Inc

Imara Inc

Invenux LLC

Ionis Pharmaceuticals Inc

Jazz Pharmaceuticals Plc

Kymab Ltd

Merganser Biotech Inc

Monte Rosa Therapeutics Inc

Nanjing Transthera Biosciences Co Ltd

Nanomedic Inc

Orchard Therapeutics Plc

Phoenicia Biosciences Inc

Rare Partners Srl

Regenacy Pharmaceuticals LLC

San Rocco Therapeutics LLC

Sana Biotechnology Inc

Sangamo Therapeutics Inc

Sanquin Plasma Products BV

Shanghai Bioray Laboratory Inc

Silence Therapeutics Plc

Suzhou GenAssist Therapeutics Co Ltd

Syros Pharmaceuticals Inc

Vera Therapeutics Inc

Vertex Pharmaceuticals Inc

Vifor Pharma Ltd

Table of Contents

Table of Contents

Introduction

Thalassemia - Overview

Thalassemia - Therapeutics Development

Thalassemia - Therapeutics Assessment

Thalassemia - Companies Involved in Therapeutics Development

Thalassemia - Drug Profiles

Thalassemia - Dormant Projects

Thalassemia - Discontinued Products

Thalassemia - Product Development Milestones

Appendix

List of Tables

List of Tables

Number of Products under Development for Thalassemia, 2021

Number of Products under Development by Companies, 2021

Number of Products under Development by Companies, 2021 (Contd..1)

Number of Products under Development by Companies, 2021 (Contd..2)

Number of Products under Development by Universities/Institutes, 2021

Products under Development by Companies, 2021

Products under Development by Companies, 2021 (Contd..1)

Products under Development by Companies, 2021 (Contd..2)

Products under Development by Companies, 2021 (Contd..3)

Products under Development by Universities/Institutes, 2021

Number of Products by Stage and Target, 2021

Number of Products by Stage and Mechanism of Action, 2021

Number of Products by Stage and Route of Administration, 2021

Number of Products by Stage and Molecule Type, 2021

Thalassemia – Pipeline by Abfero Pharmaceuticals Inc, 2021

Thalassemia – Pipeline by Acceleron Pharma Inc, 2021

Thalassemia – Pipeline by Agios Pharmaceuticals Inc, 2021

Thalassemia – Pipeline by Aruvant Sciences Inc, 2021

Thalassemia – Pipeline by ASC Therapeutics Inc, 2021

Thalassemia – Pipeline by Beam Therapeutics Inc, 2021

Thalassemia – Pipeline by Bellicum Pharmaceuticals Inc, 2021

Thalassemia – Pipeline by BGI Genomics Co Ltd, 2021

Thalassemia – Pipeline by Biomac Lifesciences Pvt Ltd, 2021

Thalassemia – Pipeline by bluebird bio Inc, 2021

Thalassemia – Pipeline by Cell Source Inc, 2021

Thalassemia – Pipeline by Cetya Therapeutics Inc, 2021

Thalassemia – Pipeline by CRISPR Therapeutics AG, 2021

Thalassemia – Pipeline by CSL Ltd, 2021

Thalassemia – Pipeline by Disc Medicine Inc, 2021

Thalassemia – Pipeline by DisperSol Technologies LLC, 2021

Thalassemia – Pipeline by EdiGene Inc, 2021

Thalassemia – Pipeline by Editas Medicine Inc, 2021

Thalassemia – Pipeline by EmeraMed Ltd, 2021

Thalassemia – Pipeline by Forma Therapeutics Inc, 2021

Thalassemia – Pipeline by Fulcrum Therapeutics Inc, 2021

Thalassemia – Pipeline by Gamida Cell Ltd, 2021

Thalassemia – Pipeline by Gilead Sciences Inc, 2021

Thalassemia – Pipeline by Hangzhou Zede Pharmaceutical Technology Co Ltd, 2021

Thalassemia – Pipeline by Imago BioSciences Inc, 2021

Thalassemia – Pipeline by Imara Inc, 2021

Thalassemia – Pipeline by Invenux LLC, 2021

Thalassemia – Pipeline by Ionis Pharmaceuticals Inc, 2021

Thalassemia – Pipeline by Jazz Pharmaceuticals Plc, 2021

Thalassemia – Pipeline by Kymab Ltd, 2021

Thalassemia – Pipeline by Merganser Biotech Inc, 2021

Thalassemia – Pipeline by Monte Rosa Therapeutics Inc, 2021

Thalassemia – Pipeline by Nanjing Transthera Biosciences Co Ltd, 2021

Thalassemia – Pipeline by Nanomedic Inc, 2021

Thalassemia – Pipeline by Orchard Therapeutics Plc, 2021

Thalassemia – Pipeline by Phoenicia Biosciences Inc, 2021

Thalassemia – Pipeline by Rare Partners Srl, 2021

Thalassemia – Pipeline by Regenacy Pharmaceuticals LLC, 2021

Thalassemia – Pipeline by San Rocco Therapeutics LLC, 2021

Thalassemia – Pipeline by Sana Biotechnology Inc, 2021

Thalassemia – Pipeline by Sangamo Therapeutics Inc, 2021

Thalassemia – Pipeline by Sanquin Plasma Products BV, 2021

Thalassemia – Pipeline by Shanghai Bioray Laboratory Inc, 2021

Thalassemia – Pipeline by Silence Therapeutics Plc, 2021

Thalassemia – Pipeline by Suzhou GenAssist Therapeutics Co Ltd, 2021

Thalassemia – Pipeline by Syros Pharmaceuticals Inc, 2021

Thalassemia – Pipeline by Vera Therapeutics Inc, 2021

Thalassemia – Pipeline by Vertex Pharmaceuticals Inc, 2021

Thalassemia – Pipeline by Vifor Pharma Ltd, 2021

Thalassemia – Dormant Projects, 2021

Thalassemia – Dormant Projects, 2021 (Contd..1)

Thalassemia – Discontinued Products, 2021

List of Figures

List of Figures

Number of Products under Development for Thalassemia, 2021

Number of Products under Development by Companies, 2021

Number of Products under Development by Universities/Institutes, 2021

Number of Products by Top 10 Targets, 2021

Number of Products by Stage and Top 10 Targets, 2021

Number of Products by Top 10 Mechanism of Actions, 2021

Number of Products by Stage and Top 10 Mechanism of Actions, 2021

Number of Products by Routes of Administration, 2021

Number of Products by Stage and Routes of Administration, 2021

Number of Products by Top 10 Molecule Types, 2021

Number of Products by Stage and Top 10 Molecule Types, 2021

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